Gene Therapy’s Promise: Future Uses, Applications & Prospects
About 320 million people worldwide live with a rare genetic disease.1 By unlocking the promise of gene therapy for millions worldwide, Pfizer is pioneering breakthroughs that will change patients’ lives.
Gene therapy could enable patients to live without the need for ongoing treatments or the burden of daily disease management.2 We’re going beyond helping people manage their diseases. We want them to thrive in every stage of life.
1. Global Genes. RARE Facts. https://globalgenes.org/rare-facts/. Accessed February 10, 2020.
2. NIH Genetics Home Reference (GHR). What is Gene Therapy? https://ghr.nlm.nih.gov/primer/therapy/genetherapy. Accessed February 10, 2020.
3. NIH National Human Genome Research Institute. Genetic Disorders. https://www.genome.gov/For-Patients-and-Families/Genetic-Disorders. Accessed February 10, 2020.
4. NIH Genetics Home Reference (GHR). What is a Gene? https://ghr.nlm.nih.gov/primer/basics/gene. Accessed February 10, 2020.
5. Forbes. How Many Possible Combinations of DNA Are There? https://www.forbes.com/sites/quora/2017/01/20/how-many-possible-combina…. Accessed February 10, 2020.
6. NIH Genetics Home Reference. How does Gene Therapy Work? https://ghr.nlm.nih.gov/primer/therapy/procedures. Accessed February 10, 2020.
7. Data on file. Pfizer Inc, New York, NY.
8. Mingozzi F, High KA. Immune responses to AAV vectors: overcoming barriers to successful gene therapy. Blood. 2013;122(1):23-36.
9. Payne J. Antibody and antigen tests. Patient Platform Limited Web site. https://patient.info/health/antibody-and-antigen-tests. Accessed February 10, 2020.