Careers
Investors
News
Partners

Health Professionals
Connect with Us

Your Health
Healthy Living
Brain & Nervous System
Cardiovascular Health
Cold & Flu
Digestive Health
Healthier Aging
Living Tobacco Free
Men’s Health
Mental Health
Nutrition & Fitness
Pediatric Health
Respiratory Health
Skin Health
Vaccines & Prevention
Women’s Health
Disease & Condition
Cancer
Acute Myeloid Leukemia (AML) Information, Diagnosis and Treatment
Cardiovascular Diseases & Conditions
Diabetes & Metabolic Disorders
Immune System Diseases & Conditions
Infections & Infectious Diseases
Neurological Diseases & Conditions
Menopause
Rare Disease
Vaccine-Related Conditions
Skin Diseases & Conditions
Managing your health
Caregiving
Evaluating Health Information
Tracking Your Health
Your Medicines
Health Literacy
Wellness
Hot Topics
Hot Topics
Exposing RA Through Photography
Our Science
Driven to Discover the cure
Focus Areas
Internal Medicine
Inflammation & Immunology
Oncology
Rare Disease
Vaccines
Anti-Infectives
Our Commitment to Address AMR
What are Anti-Infectives
Antimicrobial Resistance
A Global Anti-Infectives Leader
Antimicrobial Surveillance
Antimicrobial Stewardship
Environmental Protection in the Manufacture, Use and Disposal of Our Medicines
Product Pipeline
Clinical Trials
What are Clinical Trials?
How Clinical Trials are Conducted
Find a trial
Clinical Innovation
Pediatric Research
Trial Data & Results
Post Marketing Commitments
Pediatric Trials
R&D Platforms
Biosimilars
Gene Therapy
Medicinal Sciences
Precision Medicine
Collaboration
Competitive Grants
Independent Grants
Compound Transfer Program
Partner with Pfizer
Research sites
Hot Topics
Maternal Immunization: Protecting the Most Vulnerable Children
A Picture of Pain
Our People
Meet The Experts
Scientists
Internal Medicine – Metabolic Disease
Inflammation & Immunology
Oncology
Rare Disease
Vaccines
Medical Professionals
The Journey
Leadership
Executives
Board Members
Company Fact Sheet
Diverse Perspectives
Diversity & Inclusion
Supplier Diversity
Hot Topics
Getting to Know Jeff Settleman
The People Behind Your Vaccine
Our Purpose
Commitment to Global Health
Expanding Access
Strengthening Health Systems
Providing Disaster & Humanitarian Relief
Unleashing the Power of Our Colleagues
Highlighting Individual Voices
Protecting People and the Environment
Pfizer's Green Journey
Product Stewardship
EHS Governance
EHS Supply Chain
Key Performance Indicators
Health & Safety
Positions on Health Policies
Ready for Cures
How does Pfizer price medicines?
Value of Medicines
Policy Positions
Transparency
Working with Health Care Professionals
Transparency in Grants
Code of Conduct
Corporate Compliance
Sales and Marketing Compliance
Independent Grants
Investigator Sponsored Research
Quality Improvement
Independent Medical Education
Competitive Grants Program
Contributions & Partnerships
Healthcare Charitable Contributions
Special Charity Events
Lobbying & Political Contributions
Hot Topics
The Value of Vaccines in Disease Prevention
Our Products
Product listing
How drugs are made
Branded vs. Generic
Biologics & Biosimilars
Commitment to Quality
Upjohn
About Upjohn
Portfolio of Brands
Manufacturing Plants
UpJohn Leadership
Distributors
Pfizer Distributors
Greenstone Distributors
Medicine Safety
Reporting Adverse Events
Making Good Treatment Choices
Partnering With Patients
Health Literacy
Medicine Safety Tips for Patients
Counterfeiting
Unused Medicines
Material Safety Data Sheets
Medical Information Contacts
Hot Topics
Universal vs. Single Payer Healthcare
Counterfeit Medicines - Is The Threat Real Or Fake

Focus Brings Depth to Our Rare Disease Approach

We bring deep scientific expertise and years of exploring emerging medical frontiers to our mission with some of the world’s leading research organizations as our partners.

You are here

Your Health / Disease & Condition / Rare Disease

Rare Disease

Gene Therapy

Pulmonary Hypertension

Transthyretin Amyloidosis

Duchenne Muscular Dystrophy

Acromegaly

Gaucher Disease

Lymphangioleiomyomatosis

Sickle Cell Disease

Growth Hormone Deficiency

Hemophilia

Footer Left Menu
YOUR HEALTH
Healthy Living
Disease & Conditions
Managing Your Health
Our Science
Therapeutic Areas
Product Pipeline
Clinical Trials
R&D Platforms
Collaboration
Research Sites
OUR PEOPLE
Meet The Experts
The Journey
Leadership
Diverse Perspectives
OUR PURPOSE
Commitment to Global Health
Positions on Health Policies
Transparency
Contributions & Partnerships
OUR PRODUCTS
Product Listing
How Drugs are Made
Distributors
Material Safety Data Sheets
Global Product Information Contacts

Footer Right Menu
Section 1
Career-seekers
Investors
News & Media
Partners
Section 2
Health Professionals
Business to Business
Change Country
Sitemap
Section 3
Twitter
Facebook
Linkedin
Instagram
Youtube
Section 4
Contact Us
Terms of Use
Privacy Policy

Copyright © 2002-2018 Pfizer Inc. All rights reserved. This information—including product information—is intended only for residents of the United States.
The products discussed herein may have different labeling in different countries.